Recent publications published by researchers at the MRC WIMM.
Editing an α-globin enhancer in primary human hematopoietic stem cells as a treatment for β-thalassemia.
Mettananda S. et al, (2017), Nat Commun, 8
Badat M. and Davies J., (2017), N Engl J Med, 376, 2093 - 2094
Badat M. et al, (2016), Int J Hematol, 104, 411 - 412
Treatment of diffuse large B-cell lymphoma with secondary central nervous system involvement: encouraging efficacy using CNS-penetrating R-IDARAM chemotherapy.
Maciocia P. et al, (2016), Br J Haematol, 172, 545 - 553
Combination-therapy with concurrent deferoxamine and deferiprone is effective in treating resistant cardiac iron-loading in aceruloplasminaemia.
Badat M. et al, (2015), Br J Haematol, 171, 430 - 432