Developing a pill to treat sickle cell disease.

Higgs D., Kassouf M.

A newly identified epigenetic modifier increases fetal hemoglobin in preclinical studies.

DOI

10.1126/science.adq3757

Type

Journal article

Journal

Science

Publication Date

05/07/2024

Volume

385

Pages

27 - 28

Keywords

Animals, Humans, Mice, Anemia, Sickle Cell, Epigenesis, Genetic, Fetal Hemoglobin, Antisickling Agents, Drug Discovery

Permalink Original publication