Fragile X Syndrome Patient–Derived Neurons Developing in the Mouse Brain Show FMR1-Dependent Phenotypes
Krzisch MA., Wu H., Yuan B., Whitfield TW., Liu XS., Fu D., Garrett-Engele CM., Khalil AS., Lungjangwa T., Shih J., Chang AN., Warren S., Cacace A., Andrykovich KR., Rietjens RGJ., Wallace O., Sur M., Jain B., Jaenisch R.