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Coupling AAV-mediated promoterless gene targeting to SaCas9 nuclease to efficiently correct liver metabolic diseases
De Caneva A., Porro F., Bortolussi G., Sola R., Lisjak M., Barzel A., Giacca M., Kay MA., Vlahovicek K., Zentilin L., Muro AF.
Type
Conference paper
Publication Date
01/12/2018
Volume
29
Pages
A115 - A115