Coupling AAV-mediated promoterless gene targeting to SaCas9 nuclease to efficiently correct liver metabolic diseases

De Caneva A., Porro F., Bortolussi G., Sola R., Lisjak M., Barzel A., Giacca M., Kay MA., Vlahovicek K., Zentilin L., Muro AF.

Type

Conference paper

Publication Date

01/12/2018

Volume

29

Pages

A115 - A115

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